FDA Launches RDCA-DAP to Accelerate Rare Disease Treatments
A new U.S. initiative, the Rare Disease Cures Accelerator-Data and Analytics Platform (RDCA-DAP), has been launched to expedite treatment innovation for rare diseases. Funded by the U.S. Food and Drug Administration (FDA), this platform aims to address the lack of approved treatments for most rare diseases by sharing patient data and standardizing new data collection.
RDCA-DAP includes data from various sources such as clinical trials, observational studies, patient registries, and real-world data. It provides workspaces for advanced analytics and data interrogation, making it easier for researchers to find and access datasets of interest. The platform was launched during a virtual workshop in September 2021, attended by over 400 rare disease stakeholders and featuring 31 speakers and panelists.
The initiative is a partnership between the National Organization for Rare Disorders (NORD), the Critical Path Institute (C-Path), and the FDA. It aims to address bottlenecks in drug development for rare diseases by promoting collaboration and candid dialogue among stakeholders. RDCA-DAP integrates disease data from multiple organizations worldwide, making it more accessible and encouraging more research while lowering costs.
RDCA-DAP is a significant step towards accelerating treatment innovation for rare diseases. By sharing patient data and promoting collaboration, it aims to bring attention to relatively neglected rare diseases, of which over 90% have no FDA-approved treatment. Interested parties can find datasets of interest and request access, or submit rare disease data through the platform's website.
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